GLUT1-deficiency syndrome

نویسندگان

چکیده

Syndróm GLUT1 deficiencie je zriedkavé neurometabolické ochorenie mozgu vznikajúce pri poruche transportu glukózy cez hematoencefalickú bariéru. Keďže mozog takmer úplne závislý od dodávky ako hlavného zdroja energie a hlavným transportérom bariéru, klasický typ ochorenia sa prejavuje závažnými dôsledkami neuroglykopénie: včasnou neurovývojovou encefalopatiou s epileptickými záchvatmi, získanou mikrocefáliou, kognitívnym deficitom rozličnými perzistentnými alebo paroxyzmálnymi motorickými (často komplexnými) prejavmi, ataxia, spasticita dystónia. Najdôležitejším diagnostickým krokom dôkaz hypoglykorachie (menej 2,2 mmol/l) v likvore zníženého pomeru likvor/sérum (väčšinou menej než 0,4). Definitívnu diagnózu však prináša molekulárne genetické vyšetrenie SLC2A1 génu. Najúčinnejšou formou liečby ketogénna diéta, ktorej utilizujú mastné kyseliny náhradný zdroj pre mozog. Z hľadiska prognózy kritickým včasné rozpoznanie tým zavedenie ketogénnej diéty.

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منابع مشابه

Report on GLUT1 Deficiency Syndrome Conference

Dr. D.C. de Vivo (Professor of Pediatrics, Colombia University, New York) opens the conference with an overview on GLUT1 deficiency syndrome (GLUT1DS) from 1991, when diagnosis of GLUT1DS was first made, until now. He describes the process of glucose metabolism in the brain. Glucose is transported across the blood-brain barrier into astrocytes and neurons by GLUT1 and GLUT3. In astrocytes, gluc...

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Paroxysmal Exercise-induced Dyskinesias Caused by GLUT1 Deficiency Syndrome

BACKGROUND Glucose transporter type 1 deficiency syndrome is due to de novo mutations in the SLC2A1 gene encoding the glucose transporter type 1. PHENOMENOLOGY SHOWN Paroxysmal motor manifestations induced by exercise or fasting may be the main manifestations of glucose transporter type 1 deficiency syndrome. EDUCATIONAL VALUE Proper identification of the paroxysmal events and early diagnos...

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Dietary Treatments and New Therapeutic Perspective in GLUT1 Deficiency Syndrome.

OPINION STATEMENT GLUT1 deficiency syndrome (GLUT1DS) results from impaired glucose transport into the brain: awareness of its wide phenotypic spectrum is a prerequisite in order to ensure an early diagnosis, treating the patients is the subsequent challenge to allow prompt compensation for the brain's lack of fuel. The ketogenic diet (KD) plays a primary role in the treatment of GLUT1DS becaus...

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OBJECTIVE To describe a characteristic paroxysmal eye-head movement disorder that occurs in infants with Glut1 deficiency syndrome (Glut1 DS). METHODS We retrospectively reviewed the medical charts of 101 patients with Glut1 DS to obtain clinical data about episodic abnormal eye movements and analyzed video recordings of 18 eye movement episodes from 10 patients. RESULTS A documented histor...

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Use of dietary therapies amongst patients with GLUT1 deficiency syndrome

PURPOSE GLUT-1 deficiency syndrome (GLUT1DS) is a neurologic disorder manifesting as epilepsy, abnormal movements, and cognitive delay. The currently accepted treatment of choice is the classic 4:1 ratio ketogenic diet. METHODS A 2-page survey was distributed to all attendees of a family-centered conference for GLUT1DS in July 2015. The surveys were completed by parents, collected anonymously...

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ژورنال

عنوان ژورنال: Neurologie pro praxi

سال: 2022

ISSN: ['1803-5280', '1213-1814']

DOI: https://doi.org/10.36290/neu.2021.076